Meliani, A., Boisgerault, F., Fitzpatrick, Z., Marmier, S., Leborgne, C., Collaud, F., Simon Sola, M., Charles, S., Ronzitti, G., Vignaud, A., van Wittenberghe, L., Marolleau, B., Jouen, F., Tan, S., Boyer, O., Christophe, O., Brisson, A. R., Maguire, C. A., & Mingozzi, F. Enhanced liver gene transfer and evasion of pre-existing humoral immunity with exosome-envelope AAV vectors, Blood Advances, October 16, 2017, Read More

György, B., Sage, C., Indzhykulian, A. A., Scheffer, D. I., Brisson, A. R., Tan, S., Wu, X., Volak, A., Mu, D., Tamvakologos, P. I., Li, Y., Fitzpatrick, Z., Ericsson, M., Breakefield, X. O., Corey, D. P., & Maguire, C. A. Rescue of Hearing by Gene Delivery to inner-ear hair cells using exome associated AAV, Molecular Therapy, February 1, 2017, Read More

Berezovskii, V. K., Born, R. T., O'Brien, M., Lafond, J. F., Arsenijevic, Y., Kenna, M. A., Maguire, C. A., & Corey, D. P. Gene Transfer with AAV9-PHP.B Rescues Hearing in a Mouse Model of Usher Syndrome 3A and Transduces Hair Cells in a Non-human Primate, Molecular Therapy - Methods & Clinical Development, November 18, 2018, Read More

Prabhakar, S., Beauchamp, R. L., Cheah, P. S., Yoshinaga, A., Haidar, E. A., Lule, S., Mani, G., Maalouf, K., Stemmer-Rachamimov, A., Jung, D. H., Welling, D. B., Giovannini, M., Plotkin, S. R., Maguire, C. A., Ramesh, V., & Breakefield, X. O. Gene replacement therapy in a schwannoma mouse model of neurofibromatosis type 2, Molecular Therapy - Methods & Clinical Development, June 22, 2022, Read More

Wassmer, S. J., Carvalho, L. S., György, B., Vandenberghe, L. H., & Maguire, C. A. Exosome-associated AAV2 vector mediates robust gene delivery into the murine retina upon intravitreal injection, Scientific Reports, March 31, 2017, Read More

Griciuc, A., Federico, A. N., Natasan, J., Forte, A. M., McGinty, D., Nguyen, H., Volak, A., LeRoy, S., Gandhi, S., Lerner, E. P., Hudry, E., Tanzi, R. E., & Maguire, C. A. Gene therapy for Alzheimer’s Disease targeting CD33 reduces amyloid beta accumulation and neuroinflammation., Human Molecular Genetics, August 17, 2020, Read More

Volak, A., LeRoy, S. G., Natasan, J. S., Park, D. J., Cheah, P. S., Maus, A., Fitzpatrick, Z., Hudry, E., Pinkham, K., Gandhi, S., Hyman, B. T., Mu, D., GuhaSarkar, D., Stemmer-Rachamimov, A. O., Sena-Esteves, M., Badr, C. E., & Maguire, C. A. Virus vector mediated genetic modification of brain tumor stromal cells after intravenous delivery, Journal of Neuro-Oncology, September 1, 2018, Read More

Hudry, E., Andres-Mateos, E., Lerner, E. P., Volak, A., Cohen, O., Hyman, B. T., Maguire, C. A., & Vandenberghe, L. H. Efficient Gene Transfer to the Central Nervous System by single-stranded Anc80L65, Molecular Therapy - Methods & Clinical Development, September 21, 2018, Read More